A Novel Therapeutic Drug for Niemann-Pick Disease Type C

Ceramide Kinase Inhibitor that Improves Intracellular Lipid Transport Disorders

Small molecule compounds that facilitate drug delivery to the brain

New deuterated flow synthesis system for drug development collaboration

Triplet Repeat Disease Treatment Drug

Cyclic pyrrole-imidazole polyamide (cPIP) selectively suppresses expression of pathogenic RNA in CAG/CTG triplet repeat neurological diseases.

Protein degrading small molecule drug for neurodegenerative disease

New chemical entities promoting degradation of ubiquitinated protein aggregates through induction of selective autophagy

NK1 receptor antagonist Development of a new treatment and prophylaxis for reflex syncope

Treatment for Gaucher disease by inhibiting microglial phagocytosis-induced neuron death

Combination of microglia activation inhibitor and TNF blocker improve neuronopathic symptoms

Liver organoid model containing human hepatocytes for pharmacokinetic assay

Original method and hepatocyte reproduced hepatobiliary function